About

Stargardt disease is the most common inherited retinal disease, caused by a faulty gene that leads to macular degeneration beginning in childhood or adolescence and progressive, irreversible vision loss. Tinlarebant is an oral drug that blocks RBP4, a protein that carries vitamin A to the eye, reducing the toxic buildup that damages the retina. By limiting that supply, tinlarebant may slow the growth of retinal lesions and help preserve vision in young people with this condition.